Venue

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Debatpodium Arminius

Museumpark 3

3015 CB Rotterdam

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Attendees: 120

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Program 2024

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Best Oral Presentation:

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1st place:

Remko Goossens (LUMC) - Functional in vitro modelling of Duchenne antisense oligonucleotide therapies using 3D muscle bundles 

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2nd place:

Manon Bouckaert (Ghent University) - Evaluation of a novel antisense oligonucleotide therapy targeting a 5’UTR mutation in the RDH12 gene 

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3rd place:

Edwin van Oosten (Radboudumc) - Personalized antisense oligonucleotide screening for a Stargardt disease patient carrying the deep-intronic c.859-506G>C ABCA4 variant using human in vitro models

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Best Poster Presentation:

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1st place:

Jack Morgan (LUMC) - Antisense oligonucleotide-mediated exon skipping treatments for neurodevelopmental disorders associated with tandem-repeat domain missense variants in ANKRD17 

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2nd place:

Sebastian Sjöström (ETH Zürich) - Allele-selective ASO Reduces Aggregation in Kidney Renal Tubules in Mice with Severe ADTKD

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3rd place:

Mariana Guimarães Ramos (LUMC) - Selection of a lead antisense oligonucleotide in hiPSC cell lines for Spinocerebellar Ataxia 3